• Rhythm Seeks FDA Approval of Setmelanotide for POMC/LEPR Deficiency
  • NORD Partners with ‘Sing Me a Story’ for July 18–20 Living Rare Forum
  • Setmelanotide Receives FDA’s Orphan Drug Status for Alström Syndrome
  • Global Rare Disease Group’s Focus: 1,000 New Therapies by 2027, Despite COVID-19
  • SERPINE-1 May Help Predict Response to Gastric Sleeve Surgery, Study Suggests
  • FTO Gene Variants Increase Risk for Extreme Obesity, Brazilian Study Suggests
  • APOA2 Gene Mutation Linked to Lower ‘Good’ Cholesterol Levels in Obesity
  • Pediatric Rare Disease Therapies Increase, But Most Repurposed, Study Finds
  • Video: BioNews’ Social Media Campaign Highlights #WhatMakesMeRare
  • Five Salt-Sensitivity Genes Identified as Potential Obesity Biomarkers
  • Parents’ Genetics, Lifestyle May Affect Their Children’s Weight, Study Suggests
  • Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29